Publication:
Access to medicines for rare diseases: beating the drum for primary ciliary dyskinesia

dc.contributor.authorKARADAĞ, BÜLENT TANER
dc.contributor.authorsCrowley, Suzanne; Azevedo, Ines; Boon, Mieke; Bush, Andrew; Eber, Ernst; Haarman, Eric; Karadag, Bulent; Kotz, Karsten; Leigh, Margaret; Moreno-Galdo, Antonio; Mussaffi, Huda; Nielsen, Kim G.; Omran, Heymut; Papon, Jean-Francois; Pohunek, Petr; Priftis, Kostas; Rindlisbacher, Bernhard; Santamaria, Francesca; Valiulis, Arunas; Witt, Michal; Yiallouros, Panayiotis; Zivkovic, Zorica; Kuehni, Claudia E.; Lucas, Jane S.
dc.date.accessioned2022-03-09T14:45:58Z
dc.date.accessioned2026-01-11T11:15:57Z
dc.date.available2022-03-09T14:45:58Z
dc.identifier.doi10.1183/23120541.00377-2020
dc.identifier.eissn2312-0541
dc.identifier.pubmed32964005
dc.identifier.urihttps://hdl.handle.net/11424/219196
dc.identifier.wosWOS:000585055100026
dc.language.isoeng
dc.publisherEUROPEAN RESPIRATORY SOC JOURNALS LTD
dc.relation.ispartofERJ OPEN RESEARCH
dc.rightsinfo:eu-repo/semantics/openAccess
dc.subjectLUNG-FUNCTION
dc.subjectAZITHROMYCIN
dc.subjectMULTICENTER
dc.subjectDIAGNOSIS
dc.subjectCHILDREN
dc.subjectDNASE
dc.titleAccess to medicines for rare diseases: beating the drum for primary ciliary dyskinesia
dc.typeeditorial
dspace.entity.typePublication
oaire.citation.issue3
oaire.citation.titleERJ OPEN RESEARCH
oaire.citation.volume6

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